Niemann-Pick disease type C (NPC) is aÌýrare progressive genetic disorderÌýcharacterized by an inability of the body to transport cholesterol and other fatty substances (lipids) inside of cells. This leads to the abnormal accumulation of these substances within various tissues of the body, including brain tissue.
The global Niemann-Pick Disease Type C (NPC) market was valued at US$ million in 2023 and is anticipated to reach US$ million by 2030, witnessing a CAGR of % during the forecast period 2024-2030.
The global pharmaceutical market is 1475 billion USD in 2022, growing at a CAGR of 5% during the next six years. The pharmaceutical market includes chemical drugs and biological drugs. For biologics is expected to 381 billion USD in 2022. In comparison, the chemical drug market is estimated to increase from 1005 billion in 2018 to 1094 billion U.S. dollars in 2022. The pharmaceutical market factors such as increasing demand for healthcare, technological advancements, and the rising prevalence of chronic diseases, increase in funding from private & government organizations for development of pharmaceutical manufacturing segments and rise in R&D activities for drugs. However, the industry also faces challenges such as stringent regulations, high costs of research and development, and patent expirations. Companies need to continuously innovate and adapt to these challenges to stay competitive in the market and ensure their products reach patients in need. Additionally, the COVID-19 pandemic has highlighted the importance of vaccine development and supply chain management, further emphasizing the need for pharmaceutical companies to be agile and responsive to emerging public health needs.
This report aims to provide a comprehensive presentation of the global market for Niemann-Pick Disease Type C (NPC), with both quantitative and qualitative analysis, to help readers develop business/growth strategies, assess the market competitive situation, analyze their position in the current marketplace, and make informed business decisions regarding Niemann-Pick Disease Type C (NPC).
Report Scope
The Niemann-Pick Disease Type C (NPC) market size, estimations, and forecasts are provided in terms of revenue ($ millions), considering 2023 as the base year, with history and forecast data for the period from 2019 to 2030. This report segments the global Niemann-Pick Disease Type C (NPC) market comprehensively. Regional market sizes, concerning products by Type, by Application, and by players, are also provided.
For a more in-depth understanding of the market, the report provides profiles of the competitive landscape, key competitors, and their respective market ranks. The report also discusses technological trends and new product developments.
The report will help the Niemann-Pick Disease Type C (NPC) companies, new entrants, and industry chain related companies in this market with information on the revenues, sales volume, and average price for the overall market and the sub-segments across the different segments, by company, by Type, by Application, and by regions.
Âé¶¹Ô´´ Segmentation
By Company
Orphazyme A/S
Cyclo Therapeutics
Johnson & Johnson
Segment by Type
Arimoclomol
Trappsol Cyclo
Miglustat (Zavesca)
Segment by Application
Hospital Pharmacies
Retail Pharmacies
By Region
North America
United States
Canada
Europe
Germany
France
UK
Italy
Russia
Nordic Countries
Rest of Europe
Asia-Pacific
China
Japan
South Korea
Southeast Asia
India
Australia
Rest of Asia
Latin America
Mexico
Brazil
Rest of Latin America
Middle East & Africa
Turkey
Saudi Arabia
UAE
Rest of MEA
Chapter Outline
Chapter 1: Introduces the report scope of the report, executive summary of different market segments (by Type, by Application, etc), including the market size of each market segment, future development potential, and so on. It offers a high-level view of the current state of the market and its likely evolution in the short to mid-term, and long term.
Chapter 2: Introduces executive summary of global market size, regional market size, this section also introduces the market dynamics, latest developments of the market, the driving factors and restrictive factors of the market, the challenges and risks faced by companies in the industry, and the analysis of relevant policies in the industry.
Chapter 3: Detailed analysis of Niemann-Pick Disease Type C (NPC) companies’ competitive landscape, revenue market share, latest development plan, merger, and acquisition information, etc.
Chapter 4: Provides the analysis of various market segments by Type, covering the market size and development potential of each market segment, to help readers find the blue ocean market in different market segments.
Chapter 5: Provides the analysis of various market segments by Application, covering the market size and development potential of each market segment, to help readers find the blue ocean market in different downstream markets.
Chapter 6, 7, 8, 9, 10: North America, Europe, Asia Pacific, Latin America, Middle East and Africa segment by country. It provides a quantitative analysis of the market size and development potential of each region and its main countries and introduces the market development, future development prospects, market space, and capacity of each country in the world.
Chapter 11: Provides profiles of key players, introducing the basic situation of the main companies in the market in detail, including product sales, revenue, price, gross margin, product introduction, recent development, etc.
Chapter 12: The main points and conclusions of the report.
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1 Report Overview
1.1 Study Scope
1.2 Âé¶¹Ô´´ Analysis by Type
1.2.1 Global Niemann-Pick Disease Type C (NPC) Âé¶¹Ô´´ Size Growth Rate by Type: 2019 VS 2023 VS 2030
1.2.2 Arimoclomol
1.2.3 Trappsol Cyclo
1.2.4 Miglustat (Zavesca)
1.3 Âé¶¹Ô´´ by Application
1.3.1 Global Niemann-Pick Disease Type C (NPC) Âé¶¹Ô´´ Growth by Application: 2019 VS 2023 VS 2030
1.3.2 Hospital Pharmacies
1.3.3 Retail Pharmacies
1.4 Study Objectives
1.5 Years Considered
1.6 Years Considered
2 Global Growth Trends
2.1 Global Niemann-Pick Disease Type C (NPC) Âé¶¹Ô´´ Perspective (2019-2030)
2.2 Niemann-Pick Disease Type C (NPC) Growth Trends by Region
2.2.1 Global Niemann-Pick Disease Type C (NPC) Âé¶¹Ô´´ Size by Region: 2019 VS 2023 VS 2030
2.2.2 Niemann-Pick Disease Type C (NPC) Historic Âé¶¹Ô´´ Size by Region (2019-2024)
2.2.3 Niemann-Pick Disease Type C (NPC) Forecasted Âé¶¹Ô´´ Size by Region (2025-2030)
2.3 Niemann-Pick Disease Type C (NPC) Âé¶¹Ô´´ Dynamics
2.3.1 Niemann-Pick Disease Type C (NPC) Industry Trends
2.3.2 Niemann-Pick Disease Type C (NPC) Âé¶¹Ô´´ Drivers
2.3.3 Niemann-Pick Disease Type C (NPC) Âé¶¹Ô´´ Challenges
2.3.4 Niemann-Pick Disease Type C (NPC) Âé¶¹Ô´´ Restraints
3 Competition Landscape by Key Players
3.1 Global Top Niemann-Pick Disease Type C (NPC) Players by Revenue
3.1.1 Global Top Niemann-Pick Disease Type C (NPC) Players by Revenue (2019-2024)
3.1.2 Global Niemann-Pick Disease Type C (NPC) Revenue Âé¶¹Ô´´ Share by Players (2019-2024)
3.2 Global Niemann-Pick Disease Type C (NPC) Âé¶¹Ô´´ Share by Company Type (Tier 1, Tier 2, and Tier 3)
3.3 Players Covered: Ranking by Niemann-Pick Disease Type C (NPC) Revenue
3.4 Global Niemann-Pick Disease Type C (NPC) Âé¶¹Ô´´ Concentration Ratio
3.4.1 Global Niemann-Pick Disease Type C (NPC) Âé¶¹Ô´´ Concentration Ratio (CR5 and HHI)
3.4.2 Global Top 10 and Top 5 Companies by Niemann-Pick Disease Type C (NPC) Revenue in 2023
3.5 Niemann-Pick Disease Type C (NPC) Key Players Head office and Area Served
3.6 Key Players Niemann-Pick Disease Type C (NPC) Product Solution and Service
3.7 Date of Enter into Niemann-Pick Disease Type C (NPC) Âé¶¹Ô´´
3.8 Mergers & Acquisitions, Expansion Plans
4 Niemann-Pick Disease Type C (NPC) Breakdown Data by Type
4.1 Global Niemann-Pick Disease Type C (NPC) Historic Âé¶¹Ô´´ Size by Type (2019-2024)
4.2 Global Niemann-Pick Disease Type C (NPC) Forecasted Âé¶¹Ô´´ Size by Type (2025-2030)
5 Niemann-Pick Disease Type C (NPC) Breakdown Data by Application
5.1 Global Niemann-Pick Disease Type C (NPC) Historic Âé¶¹Ô´´ Size by Application (2019-2024)
5.2 Global Niemann-Pick Disease Type C (NPC) Forecasted Âé¶¹Ô´´ Size by Application (2025-2030)
6 North America
6.1 North America Niemann-Pick Disease Type C (NPC) Âé¶¹Ô´´ Size (2019-2030)
6.2 North America Niemann-Pick Disease Type C (NPC) Âé¶¹Ô´´ Growth Rate by Country: 2019 VS 2023 VS 2030
6.3 North America Niemann-Pick Disease Type C (NPC) Âé¶¹Ô´´ Size by Country (2019-2024)
6.4 North America Niemann-Pick Disease Type C (NPC) Âé¶¹Ô´´ Size by Country (2025-2030)
6.5 United States
6.6 Canada
7 Europe
7.1 Europe Niemann-Pick Disease Type C (NPC) Âé¶¹Ô´´ Size (2019-2030)
7.2 Europe Niemann-Pick Disease Type C (NPC) Âé¶¹Ô´´ Growth Rate by Country: 2019 VS 2023 VS 2030
7.3 Europe Niemann-Pick Disease Type C (NPC) Âé¶¹Ô´´ Size by Country (2019-2024)
7.4 Europe Niemann-Pick Disease Type C (NPC) Âé¶¹Ô´´ Size by Country (2025-2030)
7.5 Germany
7.6 France
7.7 U.K.
7.8 Italy
7.9 Russia
7.10 Nordic Countries
8 Asia-Pacific
8.1 Asia-Pacific Niemann-Pick Disease Type C (NPC) Âé¶¹Ô´´ Size (2019-2030)
8.2 Asia-Pacific Niemann-Pick Disease Type C (NPC) Âé¶¹Ô´´ Growth Rate by Region: 2019 VS 2023 VS 2030
8.3 Asia-Pacific Niemann-Pick Disease Type C (NPC) Âé¶¹Ô´´ Size by Region (2019-2024)
8.4 Asia-Pacific Niemann-Pick Disease Type C (NPC) Âé¶¹Ô´´ Size by Region (2025-2030)
8.5 China
8.6 Japan
8.7 South Korea
8.8 Southeast Asia
8.9 India
8.10 Australia
9 Latin America
9.1 Latin America Niemann-Pick Disease Type C (NPC) Âé¶¹Ô´´ Size (2019-2030)
9.2 Latin America Niemann-Pick Disease Type C (NPC) Âé¶¹Ô´´ Growth Rate by Country: 2019 VS 2023 VS 2030
9.3 Latin America Niemann-Pick Disease Type C (NPC) Âé¶¹Ô´´ Size by Country (2019-2024)
9.4 Latin America Niemann-Pick Disease Type C (NPC) Âé¶¹Ô´´ Size by Country (2025-2030)
9.5 Mexico
9.6 Brazil
10 Middle East & Africa
10.1 Middle East & Africa Niemann-Pick Disease Type C (NPC) Âé¶¹Ô´´ Size (2019-2030)
10.2 Middle East & Africa Niemann-Pick Disease Type C (NPC) Âé¶¹Ô´´ Growth Rate by Country: 2019 VS 2023 VS 2030
10.3 Middle East & Africa Niemann-Pick Disease Type C (NPC) Âé¶¹Ô´´ Size by Country (2019-2024)
10.4 Middle East & Africa Niemann-Pick Disease Type C (NPC) Âé¶¹Ô´´ Size by Country (2025-2030)
10.5 Turkey
10.6 Saudi Arabia
10.7 UAE
11 Key Players Profiles
11.1 Orphazyme A/S
11.1.1 Orphazyme A/S Company Detail
11.1.2 Orphazyme A/S Business Overview
11.1.3 Orphazyme A/S Niemann-Pick Disease Type C (NPC) Introduction
11.1.4 Orphazyme A/S Revenue in Niemann-Pick Disease Type C (NPC) Business (2019-2024)
11.1.5 Orphazyme A/S Recent Development
11.2 Cyclo Therapeutics
11.2.1 Cyclo Therapeutics Company Detail
11.2.2 Cyclo Therapeutics Business Overview
11.2.3 Cyclo Therapeutics Niemann-Pick Disease Type C (NPC) Introduction
11.2.4 Cyclo Therapeutics Revenue in Niemann-Pick Disease Type C (NPC) Business (2019-2024)
11.2.5 Cyclo Therapeutics Recent Development
11.3 Johnson & Johnson
11.3.1 Johnson & Johnson Company Detail
11.3.2 Johnson & Johnson Business Overview
11.3.3 Johnson & Johnson Niemann-Pick Disease Type C (NPC) Introduction
11.3.4 Johnson & Johnson Revenue in Niemann-Pick Disease Type C (NPC) Business (2019-2024)
11.3.5 Johnson & Johnson Recent Development
12 Analyst's Viewpoints/Conclusions
13 Appendix
13.1 Research Methodology
13.1.1 Methodology/Research Approach
13.1.2 Data Source
13.2 Disclaimer
13.3 Author Details
Orphazyme A/S
Cyclo Therapeutics
Johnson & Johnson
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*If Applicable.